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HTA Appraisal Framework Suitable for Rare Disease Treatments

Tersimpan di:
Main Authors: Facey, K, Whittal, A, Drummond, M, Upadhyaya, S, Junghans, T, Nicod, E
Format: Report Journal
Terbitan: , 2021
Subjects:
Health Technology Assessment
Appraisal
Orphan Medicinal Products
Decision-making
Patient-reported outcomes
Outcomes-based managed entry agreements
Online Access: https://zenodo.org/record/5032615
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Daftar Isi:
  • Deliverable 10.1 of WP10 proving guidance to support consistent HTA appraisal for orphan medicinal products/rare disease treatments

Lihat Juga

  • D10.2 Guidance on Use of Patient Reported Outcome Measures in HTA Appraisals of Rare Disease Treatments
    oleh: Elena Nicod, et al.
    Terbitan: (2021)
  • Guidance on use and implementation of outcomes-based managed entry agreements for rare disease treatments
    oleh: Facey, K, et al.
    Terbitan: (2021)
  • Milestone 44 - Updated review of HTA appraisal approaches for OMPs (WS1 of IMPACT HTA WP10)
    oleh: Elena Nicod, et al.
    Terbitan: (2020)
  • Examining the impact of different country processes for appraising rare disease treatments: a case study analysis
    oleh: Amanda Whittal, et al.
    Terbitan: (2021)
  • Template for Adaptation by HTA Bodies - Patient group submission form for re-appraisal of a rare disease treatment after an Outcomes-Based Managed Entry Agreement
    oleh: Facey, Karen
    Terbitan: (2021)

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